CASE TEACHING NOTES
for
Sickle Cell Anemia

by
Debra Stamper, Department of Biology
King's College


INTRODUCTION / BACKGROUND

This case was designed to be implemented in the first semester of our introductory biology course. The majority of the students enrolled in this course are freshmen majoring in either Biology or our Pre-Physician Assistant Program. Each week, students attend three 50-minute lectures and one 50-minute problem hour. Most of the sections of the case were presented during the problem hour (although one section was done at the conclusion of a lecture period).

The different sections of this case all relate to various aspects of sickle cell anemia. In the first section, students are introduced to some of the key investigators responsible for determining the molecular basis of the disease. In the second section, students learn about the functioning of erythrocytes and are introduced to the notion that changes in the environment can influence the functioning of cells. The third section allows students to become familiar with the process of osmosis and how it can influence the sickling of the erythrocytes. In each section, students must address experimental design questions.

Fact or Fiction

This case is a work of fiction that refers to real events and people. All of the discoveries mentioned in Section 1 were made by the individuals they are attributed to, as were the observations made by Dr. Vernon Hahn described in Section 2. The time between discoveries has been dramatically condensed, however. It is true that William Castle knew of Irving Sherman's spectrophotometric observations of sickled cells, but the letter written in this case is fiction. Both Linus Pauling and William Castle were members of the same medical advisory committee and it has been reported that they discussed sickle cell anemia on a train; however, their conversation as presented in this case is fictionalized. The initial separation of HbA and HbS was done using a different technique than that presented in the case. I elected to present it as gel electrophoresis for two reasons: 1) students enrolled in the course will be doing gel electrophoresis later in the semester, and 2) some of the students are already familiar with this technique. The electrophoresis results are drawn in their correct relative position, but these specific samples are a creation of the author. Irving Sherman's experiences at Boston are completely fabricated. I have no knowledge that he ever lived in the Boston area. All graduate students mentioned are also fictional, as is the intern and patient described at the end of Section 3.

CLASSROOM MANAGEMENT / BLOCKS OF ANALYSIS

Unless otherwise noted below, students were divided into cooperative learning groups. Each group consisted of three to four students. The groups were pre-assigned by the instructor at the beginning of the semester and remained intact until the conclusion of the course.

The students were told that it would be highly beneficial to bring both their textbook (5th edition of Biology by Campbell et al.) and their lecture notes to the problem hours. Students were occasionally given supplemental material (such as overhead transparencies) with some of the sections of the case. Although the supplemental material is a nice addition, it is not required for successful completion of this case. Many introductory textbooks discuss some aspect of sickle cell anemia.

Section 1: The Investigation Begins

Learning Objectives for Section 1

After completing this section of the case, students will be able to:

Presentation of Section 1

Prior to this section's being presented, students have had lectures on the scientific method, inorganic chemistry, and organic chemistry. They have had no lectures on cellular components and have not been instructed about any aspect of sickle cell anemia. This section can be completed in a 50-minute period.

Students read the section individually. They are instructed to circle any words and/or phrases that they do not understand. After reading the section, they then assemble into their cooperative learning groups. As a group, they are asked to list all the experimental evidence that relates to sickle cell anemia, including why each piece of evidence is a significant finding. They then answer the questions posed at the end of the section. Their textbook contains a diagram of the molecular structure of the different amino acids (see Biology by Campbell, 5th ed., Figure 5.15, p. 69) which aids in answering the questions.

While the students were working, I moved around to the different groups. To initiate a conversation with each group I asked them if they would like me to clarify one of the terms they had circled. Since most of the students have not performed electrophoresis, this tends to be the most common explanation requested. For the groups that did not request electrophoresis to be explained, I asked them to explain the technique to me, filling in or modifying their explanation as needed.

I discovered that many groups had no idea where to start to answer the question relating the electrophoresis data with the data from Vernon Ingram. For these groups, I simply redirected their attention to the molecular structure of the different amino acids. This was sufficient for most of the groups that were stuck, although they still had a difficult time realizing that I wasn't going to point to a section in the textbook that simply spelled out the answer. After a few minutes of grumbling about the need to do their own thinking, they would finally figure it out.

At the end of the class, each group turned in a list of experimental evidence and answers to the questions.

Suggested Answers to Questions Posed in Section 1

  1. Why did Dr. Castle not tell Dr. Pauling initially which samples came from the sickle-celled individuals?

    In order to not bias the outcome. (This question gives me the opportunity to discuss blind versus double-blind experiments.)

  2. From these results what level(s) of protein structure of the hemoglobin is altered in the sickled-cell condition? Explain the basis for your answer.

    Since there is a difference of one amino acid in the linear sequence of this protein, the primary level of structure will be altered. Altering the primary structure of any protein can then lead to possible (although not mandatory) changes in all other levels of protein structure.

  3. Are Linus Pauling's results supported by Vernon Ingram's results? Hint: compare the molecular composition of the different amino acids implicated.

    Yes, the glutamic acid carries a negative charge and would therefore migrate to the positive pole quicker.

  4. Explain the electrophoretic results of sample 48WC12.

    This sample is from an individual that possesses both forms of the hemoglobin protein. From this question you can then discuss whether this individual would have sickle cell anemia or not. This may lead to a discussion of what actually constitutes an "illness."

Section 2: To Sickle or Not to Sickle: What's a Cell to Do?

Learning Objectives for Section 2

After completing this section of the case, students will be able to:

Presentation of Section 2

Prior to being presented with this section, students had been given lectures on the various organelles found within a cell and the structure of the plasma membrane. They had not received the lectures on membrane transport. They were directed to a photo in their textbook (see Biology by Campbell, 5th edition, Figure 5.19, p. 72) comparing the microscopic appearance of red blood cells from a normal individual and those from an individual with sickle cell anemia. They were also shown an overhead transparency of a photo of normal red blood cells passing through a capillary (from Understanding Sickle Cell Disease by M. Bloom, Figure 3.1, p. 40). This photo depicts the red blood cells passing through a capillary in single-file, bending into a bullet shape in order to "squeeze" through.

This section is broken down into three distinctive parts. The students receive Parts A and B in one class and Part C the next. Students must finish Part A prior to receiving Part B. Many of the groups required the entire 50 minutes to complete Part A. Because the first part took so long to complete, Part B was given to the students as homework to do either individually or as a group. A couple of the groups were able to complete both Parts A and B during the 50-minute period. The vast majority of the students who completed Part B outside the class period worked in their cooperative learning groups. Only four of the 31 students in the class elected to work independently; at least two of these students had outside commitments that hindered their ability to meet with other students outside of class.

Most of the students had difficulty initially addressing the questions in Part A. This was related to their expectation that the answers to the questions would simply be found in the textbook. Most groups were able to generate limitations for cells without a nucleus, but had a harder time coming up with any benefits. I talked to the groups who had difficulty with this a little more about the developmental process that erythrocytes undergo. Often I commented that since the cells lose the nucleus just prior to entering the plasma, that this may enhance their functioning in the plasma. If that didn't work, I redirected their attention to the overhead (which was displayed throughout the entire period).

Part C was done separately during the last 15 minutes of a lecture period. It was during this section of the case that many of the students realized that they could answer the question being posed (even if the answer wasn't given in the textbook).

Suggested Answers to Questions Posed in Section 2

Part A

  1. Red blood cells found in the plasma of mammals do not contain a nucleus. List all the possible benefits and limitations imposed on these cells by not having a nucleus.

    The major limitation that most students are able to come up with is the inability for RBCs to continue synthesizing new proteins (over a prolonged period). I usually request that they describe what impact this would have on the functioning of the cell. The benefit to the RBC is that it is more flexible, which allows it to "squeeze" through the capillaries better.

  2. Predict how the sickling of red blood cells could impair their functioning.

    A sickled RBC will not be as flexible as a normal RBC. This may lead to the sickled cells being unable to readily traverse the narrow capillaries.

  3. Predict how the average life span of a nerve cell located in the brain differs from the average life span of a red blood cell. Provide a basis, based on cellular features, for your prediction.

    The life span of a cell located in the nerve cell should be longer since these cells retain their nucleus.

  4. It has been observed (using an electron microscope) that when the red blood cells are sickled there are little spikes that puncture the plasma membrane. Predict how this will affect the functioning of sickled cells and their life span?

    As the spikes puncture the plasma membrane, the membrane will become more permeable. This may result in the cell not being able to regulate what molecules pass across the membrane, resulting in a disturbance in the intracellular concentration of many molecules. This could also result in reducing the life span of the RBCs.

Part B

  1. How was the environment of the blood different at the top of the tube versus the bottom of the tube? Parameters to consider should include such things as: density of cells; concentration of nutrients, waste products, gases; pressure differences; and possible temperature differences.

    Initially all the variables should be equal, but over time the RBCs will sink to the bottom of the tube since they are denser than plasma. Since the density of the cells will increase at the bottom, it would be expected that at the bottom of the tube the nutrients will be lower (RBCs utilizing them) and there would be an increase in waste products (generated by the RBCs). The pressure at the bottom of the tube will be greater (due to the height of the column of plasma). Temperature should be relatively the same due to the high thermal capacity of water (it should be able to readily absorb any metabolic heat generated by the cells).

  2. How would shaking the tube alter the environment of the tube? Consider what would happen to the concentration of different molecules.

    Shaking the tube would help to re-equilibrate the contents of the bottom versus the top of the tube.

  3. What environmental factor do you believe is responsible for causing the cells to sickle?

    It has been shown that the major environmental factor is a decrease in the concentration of oxygen. Since the students do not have this information at hand, I am relatively lenient in allowing any sensible answer.

  4. How would the repeated sickling and unsickling of the cells affect the average life span of red blood cells?

    Cells that undergo repeated sickling have a reduced life span, most likely due to problems involving membrane selectivity.

Part C

  1. Why did Dr. Hahn need to test the ghosts?

    As a control. He needed to establish that it was the hemoglobin molecule that was responsible for the sickling and not some other component of the cell (such as the membrane or cytoskeleton).

Section 3: Throwing Water at the Problem

Learning Objectives for Section 3

After completing this section of the case, students will be able to:

Presentation of Section 3

This section of the case is presented to the students after the lectures on membrane transport. It is given to the students to work on in their cooperative learning groups during a 50-minute problem hour. They are instructed that in order to complete the second half of the section (the clinical problem), they must first be able to answer questions 1 through 6. At the end of the period, each group turns in their answers to the questions.

Areas in which students needed some additional guidance included determining which molecules dissociate in water and how changes in the volume of water contained within the plasma membrane of a cell can alter the concentration of intracellular molecules (such as hemoglobin).

Suggested Answers to Questions Posed in Section 3

  1. Calculate the osmolarity of each of the solutions tested.

    500 mM sucrose = 500 mosm sucrose; 300 mM NaCl = 600 mosm NaCl; 100 mM NaCl = 200 mosm NaCl; and saline is approximately 300 mosm.

  2. Determine the tonicity of each of the solutions tested.

    Saline is isotonic; both the 300 mM NaCl and 500 mM sucrose solutions are hypertonic; and the 100 mM NaCl solution is hypotonic.

  3. Compare the solute and water concentration of each solution to the solute and water concentration found within the red blood cells.

    For both the sucrose and the 300 mM NaCl solutions, the extracellular concentration of solutes is greater than the intracellular concentration and the intracellular water concentration is greater than the extracellular concentration. The intracellular and extracellular concentrations of both total solutes and water should be relatively equal for the saline solution. With the 100 mM NaCl solution, the intracellular solute concentration should be greater than the extracellular concentration and the extracellular water concentration should be greater than the intracellular concentration.

  4. Describe what should happen to the red blood cells after they were placed into each of the solutions. Include in your answer the movement of water and any possible changes to the shape of the cell. Rank the cells from each solution in terms of their volume (starting with the largest cells to the smallest cells).

    Placing the RBCs into saline solution should result in no change in their shape/size since there should be an equal amount of water moving into the cell as out of the cell. With the hypertonic solutions, the cells should get smaller since water will be moving down its concentration gradient (via osmosis) and will leave the cell. The reverse will be true for the hypotonic solution (cells will get bigger and may possibly lyse). (I always emphasize that cells will not automatically lyse if placed in a hypotonic solution.)

  5. Assuming that hemoglobin (Hb) does not leave the cell and that all red blood cells start with the same amount of Hb molecules, compare the concentration of hemoglobin found within the cells that will change after they have been placed in each of the test solutions.

    The change in hemoglobin concentration is dependent upon the amount of water present in the cell. As water leaves the cell (as in the case with the hypertonic solution), Hb will become more concentrated within the cell. If there is a net inward flux of water (as with the hypotonic solution), then the concentration of Hb will decrease.

  6. What conclusions (if any) can you draw from these results about the influence of the concentration of hemoglobin on the sickling of the cells?

    As the concentration of hemoglobin increases there is a decrease in the time required for the initiation of sickling.

  7. Which of the following solutions [saline solution, 100 mM NaCl solution, and distilled water] do you think Peter is most likely to try? Be sure to give the basis for your answer.

    (See answer under question 8).

  8. For each of the above solutions, list any possible side-effects that the may occur after the patient has been infused.

    Peter should try to use the 100 mM NaCl solution. With this solution there should be a net movement of water into the cells that would result in a decreased concentration of Hb. This may help to reduce the sickling. One possible drawback to this is that you may have some lysis of the cells, but hopefully this would be minimal. Saline would not help the situation, nor should it lead to any further complications. Distilled water would lead to more lysis of the cells than the 100 mM NaCl solution due to the greater inward flux of water (due to the higher concentration gradient). While there would be a reduction in Hb concentration within intact cells, there would be an increase in Hb concentration found in the plasma (which is detrimental to the functioning of the kidneys).


POSSIBLE "ADD-ONS" TO THE CASE

Genetics Problems

Since sickle cell anemia is a heritable trait, it is easy to continue this case into the genetics component of the class. Instead of writing another section to the case, I was interested in seeing if the students could continue on their own. Following the lectures on genetics, I included the following question on their lecture exam:

Sickle cell anemia occurs in individuals who are homozygous recessive. Individuals who are either homozygous dominant or heterozygous do not have the disease. Heterozygous individuals are said to have sickle cell trait since they are carriers. These carriers usually show no ill effects during their lifetime. However, if they find themselves in a situation where oxygen is limited (such as at high altitude), some of their red blood cells may show signs of sickling. Is this an example of complete dominance, codominance, or incomplete dominance? Provide a basis for your choice.

In their answer I expect to see something along the lines that since the phenotype of the heterozygous condition is not exactly like either of the homozygous conditions, then it should be an example of codominance.

I also had a section on their final exam (which is a comprehensive exam) that addressed different aspects of sickle cell anemia. For this exam, I give them a number of study questions which I draw upon to write the exam. Below are the study questions that I gave the class to coincide with this case. During the final exam, students are given a copy of the genetic code.

Study Questions

Sickle cell anemia is the expression of a recessive allele for a gene (which follows Mendelian genetics). Individuals who are heterozygous for this gene have the sickle cell trait.

  1. In normal individuals the sixth amino acid of hemoglobin is encoded by the codon "GAG," whereas in individuals with the recessive allele the sixth amino acid is encoded by the codon "GUG." What difference will this make in the primary structure of the protein?

  2. This change in the primary structure of the protein will end up making changes in the 3-D structure of the hemoglobin protein. Be able to describe all levels of protein structure, from primary to quarternary.

  3. Be able to determine the genotype of different individuals based upon whether they are normal, have sickle cell trait, or have sickle cell anemia? Use the letter "A" for this gene.

  4. Be able to use a Punnett Square to make genetic predictions on the mating outcomes of different individuals. Be able to do this for when you are interested in just the hemoglobin gene or when you are interested in 2 different genes (such as the hemoglobin gene and a gene on a different chromosome that encodes for the ability to curl your tongue).

  5. Describe why the inheritance of the gene for the beta subunit of hemoglobin is an example of incomplete dominance.

  6. Be able to make comparisons between a normal individual, someone with the sickle cell trait, and a person with sickle cell anemia in terms of the concentration of HbA and HbS in their red blood cells. How would these differences influence the rate at which their red blood cells would sickle?

For all of the genetics problems given to the students, the assessment of their performance was done on an individual basis.

Protein Synthesis Problem

After the lecture on translation, I gave the students the following problem set to complete during a 50-minute problem hour. Students were directed to the page in their textbook that contained the genetic code (Biology by Campbell, 5th edition, Figure 17.4, p. 299). They worked on this problem in their cooperative learning groups. At the end of the problem hour, each group turned in their answers to the questions posed.

 


Translation of Hemoglobin
(the continuation of the sickle cell saga)

Hemoglobin is a large protein molecule that consists of four subunits (2 alpha chains and 2 beta chains). Hemoglobin is synthesized within red blood cells and functions to reversibly bind oxygen molecules. The alpha and beta chains are products of two separate genes found on different chromosomes. Individuals that have sickle cell anemia have two copies of a "mutated" form of the gene that encodes for the beta subunit. This form differs from the original in only 1 nucleotide. This nucleotide difference results in a different amino acid placed in the 6th position of the protein (the mutated gene encodes for a valine residue instead of the glutamic acid encoded for by the normal gene). The protein encoded by the normal gene is designated HbA while the protein found in individuals with sickle cell anemia is HbS.

Below is the initial nucleotide sequence found in the mRNA for the beta subunit of HbA.

G U G C A C C U G A C U C C U G A G A A G (etc.)

Problems

1. Determine the primary amino acid sequence of the initial portion of the beta subunit in HbA.

Answer: Val - His - Leu - Thr - Pro - Glu - Lys

2. Determine which nucleotide is different in the mRNA for the beta subunit in HbS.

Answer: the 17th nucleotide is uracil.

 


SUPPLEMENTAL MATERIALS

Letters from Section 1 in .pdf format (requires Adobe Acrobat Reader):
Letter 1 (from Irving Sherman): letter1.pdf
Letter 2 (from Linus Pauling): letter2.pdf


REFERENCES

Books and Articles
  1. Bloom, Miriam. Understanding Sickle Cell Disease. Jackson: University Press of Mississippi, 1995.
  2. Campbell, N.A., J.B. Reece, and L.G. Mitchell. Biology, 5th ed. Menlo Park, Calif.: Benjamin Cummings, 1999.
  3. Edelstein, Stuart J. The Sickled Cell, From Myth to Molecules. Cambridge: Harvard University Press, 1986.
  4. Reid, C.D., S. Charache, and B. Lubin (eds.). Management and Therapy of Sickle Cell Disease, 3rd ed. Bethesda: National Institutes of Health; National Heart, Lung, and Blood Institute. NIH Publication #96-2117, 1995.
  5. Strasser, Bruno J. 1999. Sickle Cell Anemia: a Molecular Disease. Science 286: 1488-1490.
  6. Stryer, Lubert. Biochemistry, 2nd ed. San Francisco: W.H. Freeman & Company, 1981, 57-102.
  7. Todd, James Campbell, and Arthur Hawley Sanford. Clinical Diagnosis by Laboratory Methods, 14th ed. Edited by I. Davidson and J.B. Henry. Philadelphia: W.B. Saunders Company, 1969, 227-237.

Web Sites


Acknowledgements: This case was developed as part of a National Science Foundation-sponsored Case Studies in Science Workshop held at the State University of New York at Buffalo on June 7-11, 1999 (NSF Award #9752799).


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